National Center for Child Health and Development JAPAN（日本国立成育医疗研究中心）

个人简介:Dr. Toru Uchiyama works on the development and clinical application of gene and cell therapies. His experience includes clinical studies and investigator-initiated trials of hematopoietic stem cell gene therapy for primary immunodeficiency diseases such as chronic granulomatous disease and Wiskott-Aldrich syndrome. He has also been involved in CAR-T cell therapy for refractory leukemia, AAV-based in vivo gene therapy for neurological disorders, and genome editing-based gene therapy for primary immunodeficiency diseases. 查看更多